Alpha-Mannosidosis: Therapeutic Strategies
Abstract
:1. Introduction
2. Inherited Deficiency of Alpha-Mannosidase (Alpha-Mannosidosis)
3. Genetics of Alpha-Mannosidase
4. Therapy of Alpha-Mannosidosis
Bone Marrow Transplantation
5. Enzyme Replacement Therapy
Conflicts of Interest
References
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Ceccarini, M.R.; Codini, M.; Conte, C.; Patria, F.; Cataldi, S.; Bertelli, M.; Albi, E.; Beccari, T. Alpha-Mannosidosis: Therapeutic Strategies. Int. J. Mol. Sci. 2018, 19, 1500. https://doi.org/10.3390/ijms19051500
Ceccarini MR, Codini M, Conte C, Patria F, Cataldi S, Bertelli M, Albi E, Beccari T. Alpha-Mannosidosis: Therapeutic Strategies. International Journal of Molecular Sciences. 2018; 19(5):1500. https://doi.org/10.3390/ijms19051500
Chicago/Turabian StyleCeccarini, Maria Rachele, Michela Codini, Carmela Conte, Federica Patria, Samuela Cataldi, Matteo Bertelli, Elisabetta Albi, and Tommaso Beccari. 2018. "Alpha-Mannosidosis: Therapeutic Strategies" International Journal of Molecular Sciences 19, no. 5: 1500. https://doi.org/10.3390/ijms19051500